Microvillus inclusion disease: From organoids to new treatments
Microvillus inclusion disease (MVID) is a rare type of congenital enteropathy in infants that causes devastating diarrhea and ...
Nature14d
Microvillus Inclusion Disease And Epithelial Cell Disorders
Microvillus Inclusion Disease (MVID) is a rare congenital disorder characterized by severe diarrhea and malabsorption due to defects in the intestinal epithelial cells. This condition is part of a ...
Pharmabiz2d
Jaguar Health begins patient dosing in short bowel syndrome with intestinal failure in investigator-initiated trial of crofelemer
San Francisco, California Wednesday, February 5, 2025, 16:00 Hrs [IST] ...
Jaguar Health announces first SBS-IF patient dosed in IIT trial of crofelemer
Jaguar Health (JAGX) and Napo Therapeutics announced that the first short bowel syndrome with intestinal failure patient has been dosed in the ...
timespub11d
Avery’s Hope: Supporting Families Through the Rare Disease Journey
New Hope News - by June Portnoy In the heart of New Hope, a small nonprofit organization named Avery’s Hope is making a big ...
Hosted on MSN7mon
Child undergoes five organ transplants for rare genetic disorder
A boy from Michigan with an extremely rare genetic disorder has received five organ transplants after waiting his whole life for a match. Jakob Perez has microvillus inclusion disease (MVID ...
The Globe and Mail1mon
Phase 2 Study Initiated to Evaluate Jaguar Health's Crofelemer for Microvillus Inclusion Disease (MVID), an Ultrarare Congenital Diarrheal Disorder
The study is one of five clinical efforts - three proof-of-concept investigator-initiated trials (IIT) and two Phase 2 studies - of crofelemer for the rare disease indications of MVID and/or short ...
Stockhouse1mon
FDA Approves Orphan-Drug Designation for Jaguar Health's Crofelemer for Treatment of Diarrhea in Cholera
Crofelemer previously granted orphan-drug designation by the FDA and the European Medicines Agency (EMA) for both short bowel syndrome and microvillus inclusion disease SAN FRANCISCO, CA / ACCESSWIRE ...